Sr. Medical Science Liaison, Inborn Errors of Metabolism; Atlantic Region

Sr. Medical Science Liaison, Inborn Errors of Metabolism (Atlantic Region)

United States - Remote

Be a hero for our rare disease patients

At Ultragenyx, we fundamentally believe that taking real impactful action to care for the needs of patients and our people is always the right thing to do. To achieve this goal, our vision is to lead the future of rare disease medicine. For us, this means going where other biopharma companies won’t go – challenging the status quo and creating a new model that advances our field so more patients and caregivers can benefit from life‑changing treatments.

We do this by following the science, applying a novel rapid development approach, making innovative medicines at fair and reasonable prices, and creating a collaborative ecosystem to reach patients in ways that are most meaningful for them.

Our commitment and care for patients extends to our people, so culture is an essential cornerstone for Ultragenyx. We remain continuously focused on creating a supportive and inclusive environment of profound learning and growth – so employees can thrive in all areas of their lives, in and outside of work. Ultimately, we want to be an organization where we would be proud for our family, friends and children to work.

If you want to have a meaningful impact, do the best work of your career, and grow a lot, both professionally and personally, come join our team.

We are seeking an experienced and highly motivated Senior Medical Science Liaison (MSL) to join our team. In this role, you will serve as a key link between Ultragenyx and the rare disease medical community, delivering critical scientific information on our inborn errors of metabolism portfolio, pipeline, and products. This includes supporting preparation for the commercialization of AAV gene therapies for the treatment of glycogen storage disease type Ia (GSDIa) and mucopolysaccharidosis type IIIa (MPSIIIa).

The Sr MSL will have a strong clinical or/or scientific background, exceptional communication skills and a passion to shape the future of rare disease medicine and will interact with KOLs and centers of excellence. The Sr. MSL will also build and maintain strong partnerships with cross‑functional colleagues and work closely with the Field Medical leadership to ensure execution of the Field Medical plan.

Field:
Officially documented as working as a member of the Ultragenyx field team, generally interacting with third parties on behalf of Ultragenyx.

The territory will cover the following states: NJ, DE, DC, MD, VA, NC, SC

• Provide fair balanced presentations and medical information in response to unsolicited questions as appropriate in academic, community, and healthcare provider settings.
• Develop and execute US territory and KOL engagement plans to enable high‑quality, impactful scientific engagement and education.
• Gather and lead reporting of medical and clinical insights that contribute to enhancement of Ultragenyx’s key medical positions, plans, future research and development efforts.
• Analyze KOL’s scientific point of view on Ultragenyx’s medical and scientific positions on rare diseases and execute appropriate action plan.
• Provide field‑based medical affairs assistance for clinical research initiatives supported by the company, related to Investigator Initiated Trials or other collaborative research and initiatives.
• Collaborate with the Clinical Operations organization to enhance patient enrollment in company‑sponsored clinical trials by identifying appropriate clinical trial sites and interacting with investigators in ongoing studies.
• Lead projects/initiatives internally and represent medical affairs cross‑functionally.
• Represent Ultragenyx at scientific conferences and meetings, engaging with KOLs and collating scientific data insights. Provide leadership to plan impactful medical engagement activities and deliver timely post‑congress insight and competitive intelligence reporting.
• Partner cross‑functionally in assigned region to optimize customer experience.
• Ensure all activities are compliant with company policy and procedures, which includes documentation of all…